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June 24–26, 2020
Boston, MA

Rare Disease Innovation and Partnering Summit

Connect with Key Stakeholders and Propel Curative Progress, Orphan Product Success and Patient Advocacy

Submit a Proposal for the 2020 Program

The call for proposals is open until Friday, December 6.

Highlighted Articles

Rare Disease Article Pack

We have made available a series of articles highlighting various topics in rare disease research and regulation, and some companies involved in innovative drug development.

Download the pack
Bruce L. Levine is a man you can thank for your future cell therapy

Catch up on Bruce L. Levine's research and outlook on cell and gene therapies, and the importance of partnerships in progressing the field.

Read the article


Patient and Caregiver Perspectives
Explore New Developments in Cures, Community, Collaboration and the Care Continuum for Patients and Caregivers

Science Luminaries 
Advancements in Gene Therapy that Are Tearing Down Barriers to Discovery in Rare Disease

Regulatory and Policy Update Address
Legislative Updates and New Initiatives within the FDA’s Orphan Drug Program

Focus on Funding
The Impact of Disruptive Investors, Drivers of Value and Funding Models for Success

Technology Spotlight 
Artificial Intelligence (AI) and Advanced Data Analytics — Reshaping Complex Diagnostics and Decision-Making in Rare Disease Drug Development