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Partnerships are key for rare disease drug discovery and development

What kinds of partnerships are key to getting rare disease research out of the lab and to patients as therapies and cures? Wendy White, Board Chairman of Global Genes, discusses her work on behalf of the leading global rare disease patient advocacy organization, and the impact patient advocacy groups are making on rare disease research at BIO-Europe Spring 2017 in Barcelona, Spain.

Commercializing cell and gene therapies

New business models for clinical development and manufacturing require strategic partnerships among researchers, manufacturers and payers to fully realize the commercial opportunities.

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Can pharma afford to cure patients instead of treating them?

March 27, 2017

2016 – A Year in Review for Advanced Therapies

March 9, 2017

World RARE Disease Day shines a light on rare disease community

February 27, 2017

Unmet needs, uncommon commitment: The shift toward investment in rare diseases

January 19, 2017

The renaissance of gene therapy

January 10, 2017

The state of cell and gene therapy: Reimbursement and manufacturing dominate

January 10, 2017

Realities of Rare Disease and the Role of Patient Investors

December 16, 2017


Insight: Cell & Gene Therapies

Gene therapy and Cell therapy are overlapping fields of biomedical research with similar therapeutic goals to manipulate a patient's cells for the treatment of an inherited or acquired disease.